Date |
Product |
Disease |
Phase |
Company |
Therapeutic area |
2019-11-19
|
TX200 |
kidney transplantation |
1-2 |
Sangamo Therapeutics (USA - CA) |
Transplantation |
2019-07-29
|
genome editing using zinc finger nucleases (ZFNs) |
|
preclinical |
Sangamo Therapeutics (USA - CA) |
|
2019-07-01
|
allele-selective zinc finger protein transcription-factors (ZFP-TFs) |
Huntington's disease |
preclinical |
Sangamo Therapeutics (USA - CA) |
Rare diseases - Neurodegenerative diseases |
2019-03-28
|
VY-AADC |
Parkinson's disease |
1b |
Voyager Therapeutics (USA-MA) |
Neurological diseases - Neurodegenerative diseases |
2019-03-19
|
zinc finger protein transcription factors (ZFP-TFs) |
Tau pathology, tauopathies |
preclinical |
Sangamo Therapeutics (USA - CA) |
Neurodegenerative diseases |
2019-03-08
|
zinc finger nuclease (ZFN) platform technology |
|
preclinical |
Sangamo Therapeutics (USA - CA) |
|
2019-02-20
|
ST-920 |
Fabry disease |
1-2 |
Sangamo Therapeutics (USA - CA) |
Rare diseases - Genetic diseases |
2019-01-07
|
|
dry Age-Related Macular Degeneration (AMD) |
registry |
Gemini Therapeutics (USA) |
Ophthalmological diseases |
2019-01-07
|
VY-AADC |
Parkinson's disease |
2 |
Voyager Therapeutics (USA-MA) |
Neurological diseases - Neurodegenerative diseases |
2018-12-17
|
SB-FIX - adeno-associated virus serotype 2/6 (rAAV2/6) vectors encoding zinc finger nucleases (ZFNs) and human factor 9 gene (SB-FIX) |
hemophilia B |
1-2 |
Sangamo Therapeutics (USA - CA) |
Rare diseases - Genetic diseases - Hematological diseases |
2018-10-19
|
apceth-201 |
acute graft-versus-host disease (aGvHD) |
preclinical |
apceth (Germany) |
Transplantation |
2018-10-16
|
BI-1607 (anti FcgammaRllB antibody/anti-PD1 antibody) |
solid tumors |
preclinical |
BioInvent (Sweden) |
Cancer - Oncology |
2018-10-16
|
anti FcgammaRllB antibody/anti-PD1 antibody program |
solid tumors |
preclinical |
BioInvent (Sweden) |
Cancer - Oncology |
2018-10-16
|
BI-1808 |
solid tumors |
preclinical |
BioInvent (Sweden) |
Cancer - Oncology |
2018-10-15
|
BPS-804 (setrusumab) |
osteogenesis imperfecta (OI) |
2b |
Mereo Biopharma (UK) |
Bone diseases - Metabolic diseases - Rare diseases |
2018-10-15
|
KB103 (replication defective herpes simplex type 1 virus (HSV-1) vector expressing human COL7 protein) |
dystrophic epidermolysis bullosa |
1-2 |
Krystal Biotech (USA - PA) |
Rare diseases - Genetic diseases - Dermatological diseases |
2018-10-15
|
ARO-ANG3 |
dyslipidemia |
1 |
Arrowhead Pharmaceuticals (USA - CA) |
Metabolic diseases |
2018-10-12
|
zanubrutinib - BGB-3111 |
chronic lymphocytic leukemia, small lymphocytic lymphoma, Waldenstöm's macroglobulinemia |
1 |
BeiGene (China) |
Cancer - Oncology |
2018-10-12
|
evobrutinib - M2951 |
relapsing multiple sclerosis (RMS) |
2 |
Merck KGaA (Germany) |
Autoimmune diseases - Neurodegenerative diseases |
2018-10-12
|
Opdivo® (nivolumab) |
relapsed small cell lung cancer |
3 |
BMS (USA - NY) |
Cancer - Oncology |